Phase IIIb, Randomized Multicentre Comparative Trial to Evaluate the Long Term Effectiveness & Safety of the use of Carbaglu® in Patients with Propionic Acidemia (PA) or Methylmalonic Acidemia (MMA)

drug protocol number
IIT-OE-2013-001
drug sponsor
KAIMRC
drug study
Carglumic acid
drug trial site
NGHA-R
drug status
Ongoing
drug phase