"An Open-Label, Multicenter, Multinational Study of the Safety, Efficacy and Pharmacokinetics of Asfotase Alfa (human recombinant tissue non-specific alkaline phosphatase fusion protein) in Infants and Children ≤ 5 Years of Age with Hypophosphatasia (HPP). "

drug protocol number
ENB-010-10
drug sponsor
Alexion
drug study
Asfotase Alfa
drug trial site
KFSH & RC-R
drug status
Completed
drug phase